Gaucher disease (GD)-specific patient-reported outcome (PRO) measures for clinical monitoring and for clinical trials

被引：2
|
作者：
Elstein, Deborah [1 ]
Klemen, Martin [1 ]
Panter, Charlotte [2 ]
Bonner, Nicola [2 ]
Johnson, Chloe [2 ]
Zimran, Ari [3 ,4 ]
机构：
[1] Shire, Zug, Switzerland
[2] Adelphi Values, Macclesfield, Cheshire, England
[3] Shaare Zedek Med Ctr, Jerusalem, Israel
[4] Hebrew Univ Hadassah Med Sch, Jerusalem, Israel
来源：
MOLECULAR GENETICS AND METABOLISM | 2019年 / 126卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2018.12.117
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
101
引用
收藏
页码：S52 / S52
页数：1
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