Pharmacokinetic profile of recombinant human N-acetylgalactosamine 4-sulfatase (rhASB) enzyme replacement therapy in patients with mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)

被引：0
|
作者：
Harmatz, P
Whitley, C
Steiner, R
Plecko, B
Kaplan, P
Waterson, J
Ketteridge, D
Giugliani, R
Schwartz, I
Guffon, N
Miranda, CS
Keppen, L
Teles, EL
Kramer, WG
Hopwood, JJ
机构：
[1] Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
[2] Oregon Hlth Sci Univ, Portland, OR 97201 USA
[3] Graz Univ, Kinderklin, A-8010 Graz, Austria
[4] Childrens Hosp Philadelphia, Philadelphia, PA USA
[5] Womens & Childrens Hosp, Adelaide, SA, Australia
[6] Hospl Clin Porto Alegre, Porto Alegre, RS, Brazil
[7] Hosp Edouard Herriot, Lyon, France
[8] Univ S Dakota, Vermillion, SD 57069 USA
[9] Hosp Sao Joao, Oporto, Portugal
[10] Kramer Consulting LLC, N Potomac, MD USA
[11] Childrens Hosp & Res Ctr, Oakland, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2004年 / 81卷 / 03期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：172 / 172
页数：1
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