Development of a standard of care for patients with valosin-containing protein associated multisystem proteinopathy

被引：0
|
作者：
Korb, M. [1 ]
Peck, A. [2 ]
Berger, K. [3 ]
James, M. [4 ]
Ghoshal, N. [5 ]
Healzer, E. [6 ]
Henchcliffe, C. [1 ]
Khan, S. [7 ]
Mammen, P. [7 ]
Patel, S. [8 ]
Pfeffer, G. [9 ]
Ralston, S. [10 ]
Roy, B. [11 ]
Seeley, B. [12 ]
Swenson, A. [13 ]
Mozaffar, T. [1 ]
Weihl, C. [5 ]
Kimonis, V. [1 ]
Alfano, L. [14 ]
机构：
[1] UC Irvine Sch Med, Orange, CA USA
[2] Cure VCP Dis, Americus, GA USA
[3] NYU, Grossman Sch Med, New York, NY USA
[4] John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England
[5] Washington Univ, St Louis, MO 63110 USA
[6] Thriving Hope Consulting, Vinton, VA USA
[7] UT Southwestern Sch Med, Dallas, TX USA
[8] Wellness Sujata, Wadsworth, OH USA
[9] Univ Calgary, Cumming Sch Med, Calgary, AB, Canada
[10] Univ Edinburgh, Edinburgh, Midlothian, Scotland
[11] Yale Sch Med, New Haven, CT USA
[12] Univ Calif San Francisco, San Francisco, CA 94143 USA
[13] Univ Iowa Hosp & Clin, Iowa City, IA 52242 USA
[14] Nationwide Childrens Hosp, Columbus, OH USA
来源：
NEUROMUSCULAR DISORDERS | 2021年 / 31卷
关键词：
D O I：
10.1016/j.nmd.2021.07.372
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
EP.347
引用
收藏
页码：S155 / S156
页数：2
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