Non-Viral Gene Therapy By Liver-Directed Hydrodynamic Delivery of Sleeping Beauty Transposons to Treat Hemophilia and Mucopolysaccharidoses in Dogs

被引：1
|
作者：
Hackett, Perry B. [1 ]
Aronovich, Elena L. [1 ]
Bell, Jason B. [1 ]
Rusten, Myra [2 ]
Hunter, David W. [2 ]
Hall, Bryan C. [1 ]
Olson, Erik R. [3 ]
Hyland, Kendra A. [3 ]
Ellinwood, N. Matthew [4 ]
McIvor, R. Scott [1 ,3 ]
机构：
[1] Univ Minnesota, Genet Cell Biol & Dev, Minneapolis, MN USA
[2] Univ Minnesota, Sch Med, Intervent Radiol, Minneapolis, MN 55455 USA
[3] Discovery Genom Inc, Minneapolis, MN USA
[4] Iowa State Univ, Anim Sci & Vet Clin Sci, Ames, IA USA
来源：
MOLECULAR THERAPY | 2015年 / 23卷
关键词：
D O I：
10.1016/S1525-0016(16)33731-5
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
126
引用
收藏
页码：S52 / S52
页数：1
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