Induced Pluripotent Stem Cells as a Model To Test Gene Augmentation Therapy for Choroideremia

被引：0
|
作者：
Vasireddy, Vidyullatha [1 ]
Mills, Jason A. [2 ]
Gaddameedi, Rajashekhar [1 ]
Basner-Tschakarjan, Etiena [2 ]
Kohnke, Monica [3 ]
Black, Aaron H. [1 ]
Alexandrov, Krill [3 ]
Maguire, Albert M. [1 ,2 ]
Chung, Daniel [1 ,2 ]
Mac, Helen [2 ]
Sullivan, Lisa [4 ]
Gadue, Paul [2 ,5 ]
Bennicelli, Jeannette L. [1 ]
French, Deborah L. [2 ,5 ]
Bennett, Jean [1 ,2 ]
机构：
[1] Univ Penn, Schie Eye Inst, Philadelphia, PA 19104 USA
[2] Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA
[3] Univ Queensland, Inst Mol Biosci, St Lucia, Qld, Australia
[4] Children Hosp Philadelphia, Dept Anat Pathol, Philadelphia, PA USA
[5] Childrens Hosp Philadelphia, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA
来源：
MOLECULAR THERAPY | 2013年 / 21卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
224
引用
收藏
页码：S87 / S87
页数：1
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