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- [1] Development of new lentiviral vectors for the gene therapy of LAD-IHUMAN GENE THERAPY, 2013, 24 (12) : A39 - A39Leon-Rico, D.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, SpainAldea, M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, SpainSantilli, G.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, Mol Immunol Unit, London, England Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, SpainThrasher, A. J.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, Mol Immunol Unit, London, England Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, SpainBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, SpainAlmarza, E.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Div Hematopoiet Innovat Therapies, Madrid, Spain
- [2] Comprehensive preclinical studies for the gene therapy of patients with leukocyte adhesion deficiency type I (LAD-I)HUMAN GENE THERAPY, 2018, 29 (12) : A28 - A28Almarza, E.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, SpainMesa-Nunez, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, SpainDamian, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, SpainDiez-Cabezas, B.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, SpainFernandez-Garcia, M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, SpainBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Div Hematopoiet Innovat Therapies, Ctr Invest Energet Medioambientales & Tecnol CIEM, Madrid 28040, Spain
- [3] Disrupting the 'neutrostat' in LAD-INature Reviews Immunology, 2014, 14 (5) : 286 - 286Kirsty Minton论文数: 0 引用数: 0 h-index: 0
- [4] Gene Therapy of Patients with Leukocyte Adhesion Deficiency Type I (LAD-I): Preclinical Studies and Clinical Trial DesignMOLECULAR THERAPY, 2019, 27 (04) : 392 - 392Almarza, Elena论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainMesa-Nunez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainDamian, Carlos论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainDiez-Cabezas, Begona论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainFernandez-Garcia, Maria论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLozano, MLuz论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainRio, Paula论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainYanez, Rosa M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBeard, Brian论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut, New York, NY USA Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Pediat Oncol Hematol & Stem Cell Transplant Dept, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSchwartz, Jonathan D.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut, New York, NY USA Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain
- [5] LAD-I: a magnesium sensing deficiency?SWISS MEDICAL WEEKLY, 2022, 152 : 18S - 19SMarti, A.论文数: 0 引用数: 0 h-index: 0Lotscher, J.论文数: 0 引用数: 0 h-index: 0Grahlert, J.论文数: 0 引用数: 0 h-index: 0Hess, C.论文数: 0 引用数: 0 h-index: 0
- [6] Lentiviral Vector-Mediated Gene Complementation for the Diagnosis of LAD-IMOLECULAR THERAPY, 2020, 28 (04) : 176 - 177Mesa-Nunez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainDamian, Carlos论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGilmour, Kimberly论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Theme, London, England Great Ormond St Hosp Sick Children, Dept Immunol, London, England Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSanchez, Rebeca论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainAlberquilla, Omaira论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSegovia, Jose C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Theme, London, England Great Ormond St Hosp Sick Children, Dept Immunol, London, England Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainIp, Winnie论文数: 0 引用数: 0 h-index: 0机构: Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain UCL Great Ormond St Inst Child Hlth, Infect Immun & Inflammat Theme, London, England Great Ormond St Hosp Sick Children, Dept Immunol, London, England Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainAlmarza, Elena论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIEMAT C, Madrid, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain
- [7] Stable transduction of long-term HSCs under optimized GMP-conditions for the gene therapy of LAD-I patientsHUMAN GENE THERAPY, 2019, 30 (11) : A86 - A87Mesa-Nunez, C.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainDamian, C.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainFernandez-Garcia, M.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainDiez-Cabezas, B.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainLozano, M. L.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainRio, P.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainYanez, R.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainLaw, K.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut, New York, NY USA Hosp Infantil Univ Nino Jesus, Pediat Oncol Hematol & Stem Cell Transplant Dept, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainBeard, B.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut, New York, NY USA Hosp Infantil Univ Nino Jesus, Pediat Oncol Hematol & Stem Cell Transplant Dept, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainSchwartz, J. D.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut, New York, NY USA Hosp Infantil Univ Nino Jesus, Pediat Oncol Hematol & Stem Cell Transplant Dept, Madrid, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, SpainAlmarza, E.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain UAM, FJD, IIS, Adv Therapies Unit, Madrid 28040, Spain CIEMAT, CIBERER, Div Hematopoiet Innovat Therapies, E-28040 Madrid, Spain
- [8] Regulated CD18 expression in the haematopoietic gene therapy of leukocyte adhesion deficiency type I (LAD-I)HUMAN GENE THERAPY, 2017, 28 (12) : A22 - A22Mesa-Nunez, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainDamian, C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainLeon-Rico, D.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainAldea, M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainThrasher, A. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Coll London ICH UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, SpainAlmarza, E.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid 28040, Spain Fdn Jimenez Diaz IIS FJD UAM, Inst Invest Sanitaria, Adv Therapies Unit, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol CIEM, Div Haematopoiet Innovat Therapies, Madrid 28040, Spain
- [9] Gene Therapy for Lad-I Immunodeficiency: Preclinical Evaluation of HSC Transduction Under Optimized GMP-ConditionsBLOOD, 2019, 134Almarza, Elena论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Rara CIBERER I, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainMesa-Nunez, Cristina论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Rara CIBERER I, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainDamian, Carlos论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Rara CIBERER I, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainFernandez-Garcia, Maria论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Rara CIBERER I, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainDiez-Cabezas, Begona论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Rara CIBERER I, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainLozano, M. Luz论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Rara CIBERER I, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainRio, Paula论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainYanez, Rosa M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Ctr Invest Biomed Red Enfermedades Rara CIBERER I, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD UA, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainLaw, Ken论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, New York, NY USA Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainBeard, Brian C.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, New York, NY USA Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainSchwartz, Jonathan D.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, New York, NY USA Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, SpainBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain Inst Invest Sanitaria Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Div Hematopoiet Innovat Therapies, Madrid, Spain
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