[1] Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, I-20132 Milan, Italy
[2] Ist Sci San Raffaele, Ctr Translat Genom & Bioinformat, I-20132 Milan, Italy
[3] Univ Vita Salute San Raffaele, Sch Medecine, Milan, Italy
[4] Telethon Inst Gene Therapy TIGET, Milan, Italy