Advancing Translational Research Through the NHLBI Gene Therapy Resource Program (GTRP)

被引:4
|
作者
McDonald, Cheryl L. [1 ]
Benson, Janet [2 ]
Cornetta, Kenneth [3 ]
Diggins, Margaret [4 ]
Johnston, Julie C. [5 ]
Sepelak, Susan [4 ]
Wang, Gensheng [2 ]
Wilson, James M. [5 ]
Wright, J. Fraser [6 ,7 ]
Skarlatos, Sonia I. [1 ]
机构
[1] NHLBI, Div Cardiovasc Sci, NIH, Bethesda, MD 20892 USA
[2] Lovelace Biomed & Environm Res Inst, Albuquerque, NM 87108 USA
[3] Indiana Univ, Dept Med & Mol Genet, Indianapolis, IN 46202 USA
[4] Social & Sci Syst, Silver Spring, MD 20910 USA
[5] Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA
[6] Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA USA
[7] Univ Penn, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA
关键词
D O I
10.1089/humc.2013.036
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
Translational research is a lengthy, complex, and necessary endeavor in order to bring basic science discoveries to clinical fruition. The NIH offers several programs to support translational research including an important resource established specifically for gene therapy researchers-the National Heart, Lung, and Blood Institute (NHLBI) Gene Therapy Resource Program (GTRP). This paper reviews the core components of the GTRP and describes how the GTRP provides researchers with resources that are critical to advancing investigational gene therapy products into clinical testing.
引用
收藏
页码:5 / 10
页数:6
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