Outcomes of Allogeneic Hematopoietic Stem Cell Transplantation for Congenital Amegakaryocytic Thrombocytopenia, a PDWP/EBMT Study

被引:0
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作者
Aldebert, Clemence [1 ]
Fahd, Mony [2 ]
Galimard, Jacques-Emmanuel [3 ]
Ghemlas, Ibrahim A. [4 ]
Zecca, Marco [5 ]
Silva, Juliana [6 ]
Mohseny, Alexander [7 ]
Kupesiz, Alphan [8 ]
Hamladji, Rose-Marie [9 ]
Miranda, Nuno [10 ]
Gungor, Tayfun [11 ]
Wynn, Robert F. [12 ]
Merli, Pietro [13 ]
Sundin, Mikael [14 ,15 ]
Faraci, Maura [16 ]
Diaz-de-Heredia, Cristina [17 ]
Burkhardt, Birgit [18 ]
Bordon, Victoria [19 ]
Jubert, Charlotte [20 ]
Bader, Peter [21 ]
Ifversen, Marianne [22 ]
Arroyo, Concepcion Herrera [23 ]
Maximova, Natalia [24 ]
Riesco, Susana [25 ]
Stein, Jerry [26 ]
Dalissier, Arnaud [27 ]
Locatelli, Franco [13 ,28 ]
Kalwak, Krzysztof [29 ]
Dalle, Jean-Hugues [1 ]
Corbacioglu, Selim [30 ]
机构
[1] Univ Paris Cite, Robert Debre Hosp, GHU AP HP Nord, Pediat Hematol & Immunol Dept, Paris, France
[2] Univ Paris, Robert Debre Hosp, GH AP HP Nord, Pediat Hematol & Immunol Dept, Paris, France
[3] Sorbonne Univ, St Antoine Hosp, AP HP, EBMT Stat Unit,INSERM UMRs 938, Paris, France
[4] King Faisal Specialist Hosp & Res Ctr, Dept Pediat Hematol Oncol, Riyadh, Saudi Arabia
[5] Fdn IRCCS Policlin San Matteo, Pediat Hematol Oncol, Pavia, Italy
[6] Great Ormond St Hosp Sick Children, Bone Marrow Transplant Dept, London, England
[7] Leiden Univ, Willem Alexander Childrens Hosp, Div Stem Cell Transplantat, Med Ctr, Leiden, Netherlands
[8] Akdeniz Univ, Med Sch, Pediat Hematol, Antalya, Turkey
[9] Ctr Pierre & Marie Curie, Serv Hematol Greffe MoeIle, Algiers, Algeria
[10] Inst Portugues Oncol Francisco Gentil, BMT, Lisbon, Portugal
[11] Univ Childrens Hosp, Hosp Eleonore Fdn, Div Stem Cell Transplantat, Zurich, Switzerland
[12] Royal Manchester Childrens Hosp, Dept Paediat Haematol, Bone Marrow Unit, Manchester, Lancs, England
[13] IRCCS Bambino GesU Childrens Hosp, Dept Pediat Hematol Oncol Cell & Gene Therapy, Rome, Italy
[14] Karolinska Univ Hosp, Astrid Lindgren Childrens Hosp, Div Pediat Hematol Immunol & HCT, Pediat Hematol Immunol & HCT Sect, Stockholm, Sweden
[15] Karolinska Inst, Div Pediat, CLINTEC, Stockholm, Sweden
[16] IRCSS, Dept Hematol Oncol & Hematopoiet Stem Cell Transp, Unita Trapianto Cellule Staminali Emopoiet, Ist Giannina Gaslini, Genoa, Italy
[17] Hosp Univ Vall dHebron Vall dHebron, Pediat Oncol & Hematol Dept, Barcelona, Spain
[18] Univ Hosp Munster, Pediat Hematol & Oncol, Munster, Germany
[19] Ghent Univ Hosp, Dept Pediat Hematol Oncol & Stem Cell Transplanta, Ghent, Belgium
[20] CHU Bordeaux, Hematol Pediat, Bordeaux, France
[21] Univ Childrens Hosp Frankfurt, Dept Children & Adolescents, Div Stem Cell Transplantat Immunol & Intens Care, Frankfurt, Germany
[22] Copenhagen Univ Hosp, Dept Paediat & Adolescent Med, Rigshosp, Copenhagen, Denmark
[23] Univ Cordoba, Dept Hematol, Reina Sofia Univ Hosp, Cordoba, Spain
[24] Inst Maternal & Child Hlth IRCCS Burlo Garofolo, Bone Marrow Transplant Ctr, Trieste, Italy
[25] Hosp Univ Salamanca IBSAL, Dept Pediat, Salamanca, Spain
[26] Schneider Childrens Med Ctr Israel, Dept Hematooncol, Petah Tiqwa, Israel
[27] Sorbonne Univ, EBMT Paris Study Unit, St Antoine Hosp, AP HP,INSERM UMRs 938, Paris, France
[28] IRCCS Bambino GesU Childrens Hosp, Dept Pediat Hematol Oncol, Cell & Gene Therapy, Rome, Italy
[29] Wroclaw Med Univ, Dept Pediat Hematol, Oncol & Bone Marrow Transplantat, Wroclaw, Poland
[30] Univ Regensburg, Dept Pediat Hematol Oncol & Stem Cell Transplanta, Regensburg, Germany
关键词
D O I
10.1182/blood-2022-166636
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:10895 / 10896
页数:2
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