Y Gene modified hematopoietic stem cell transplantation for mucopolysaccharidosis type IIIC

被引：0
|
作者：
Badell-Grau, Rafael A. [1 ]
Sivakumar, Anusha [1 ]
Pakravesh, Kasra [1 ]
Chen, Rola [1 ]
Duong, Kalvin [1 ]
Losay, Pauline [1 ]
Khare, Veenita [1 ]
Thai, Kevin E. [1 ]
Pithia, Rushil [1 ]
Son, Frankie [1 ]
Corl, Alexis N. [1 ]
Tran, Christine [1 ]
Cherqui, Stephanie [1 ]
机构：
[1] Univ Calif San Diego, La Jolla, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107764
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
25
引用
收藏
页数：1
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