Understanding the Real-World Clinical Effectiveness of Pegcetacoplan for the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH)

被引:0
|
作者
Fishman, Jesse [1 ]
Rich, Carly [2 ]
Wilson, Koo [2 ]
Mellor-Bowman, Jennifer [3 ]
Earl, Lucy [3 ]
Taylor, Yasmin [3 ]
Simons, Alice [3 ]
Conyers, Joe [3 ]
机构
[1] Apellis Pharmaceut Inc, Waltham, MA USA
[2] Swedish Orphan Biovitrum AB, Stockholm, Sweden
[3] Adelphi Real World, Bollington, England
来源
关键词
PNH; pegcetacoplan; C3; inhibitor; real-world; survey;
D O I
暂无
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
MDS-539
引用
收藏
页码:S369 / S370
页数:2
相关论文
共 50 条
  • [1] UNDERSTANDING THE REAL-WORLD CLINICAL EFFECTIVENESS OF PEGCETACOPLAN FOR THE TREATMENT OF PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)
    Fishman, J.
    Rich, C.
    Wilson, K.
    Mellor, J.
    Earl, L.
    Taylor, Y.
    Conyers, J.
    Simons, A.
    VALUE IN HEALTH, 2023, 26 (06) : S56 - S56
  • [2] Real-world experience of pegcetacoplan in paroxysmal nocturnal hemoglobinuria
    Griffin, Morag
    Kelly, Richard
    Brindel, Isabelle
    Maafa, Lynda
    Trikha, Roochi
    Muus, Petra
    Munir, Talha
    Varghese, Abraham Mullasseril
    Mitchell, Lindsay
    Nagumantry, Sateesh
    Gandhi, Shreyans
    Pike, Alex
    Kulasekararaj, Austin G.
    de Latour, Regis Peffault
    AMERICAN JOURNAL OF HEMATOLOGY, 2024, 99 (05) : 816 - 823
  • [3] A First Report from the COMPLETE Study on the Real-World Effectiveness of Pegcetacoplan in Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH)
    de Latour, Regis Peffault
    Trikha, Roochi
    Gonzalez, Carmen Gonzalez
    Nolte, Matthias
    Malmstrom, Hakan
    Lethagen, Stefan
    BLOOD, 2024, 144 : 5669 - 5670
  • [4] A REAL-WORLD ANALYSIS OF TREATMENT ADHERENCE AND CLINICAL OUTCOMES FOR PATIENTS WITH PAROXYSMAL NOCTURNAL HAEMOGLOBINURIA (PNH) RECEIVING PEGCETACOPLAN
    Wilson, Koo
    Rich, Carly
    Hakimi, Zalmai
    Horneff, Regina
    Fishman, Jesse
    Mellor, Jennifer
    Earl, Lucy
    Taylor, Yasmin
    Simons, Alice
    BONE MARROW TRANSPLANTATION, 2024, 59 : 190 - 191
  • [5] Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) Treated with Pegcetacoplan: Real Life Experience
    Vallejo, Carlos
    Bonanad Boix, Santiago
    Carnicero, Fernando
    Gaya, Anna
    Pilar Gonzalez, Ana
    Gonzalez Fernandez, Fernando Ataulfo
    Lavilla, Esperanza
    Jose Salido, Eduardo
    Sanchez Anton, Piva
    Vara, Miriam
    BLOOD, 2023, 142
  • [6] Real-World Study of US Adults with Paroxysmal Nocturnal Hemoglobinuria Treated with Pegcetacoplan
    Mulherin, Brian
    Shenoy, Apeksha
    Arnett, Lily
    Jiao, Weiqi
    Guarinoni, Joseph
    Sarda, Sujata
    Min, Jinny
    Dingli, David
    HEMATOLOGY REPORTS, 2024, 16 (04) : 669 - 681
  • [7] A Real-World Evidence Review of Post-Marketing Safety and Compliance with Pegcetacoplan in Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) in the US
    de Castro, Carlos M.
    Dingli, David
    Al-Adhami, Mohammed
    Mulherin, Brian
    Yeh, Michael
    Lallier, Stacie
    Fishman, Jesse
    BLOOD, 2023, 142
  • [8] Real-World Treatment Outcomes of Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients Treated with Pegcetacoplan and Complement Protein 5 Inhibitors (C5i)
    Majerus, Elaine M.
    Mulherin, Brian
    Wilson, Koo
    Fishman, Jesse
    Mellor, Jennifer
    Earl, Lucy
    Roeth, Alexander
    BLOOD, 2023, 142
  • [9] Work Productivity and Activity Impairment (WPAI), and Hemoglobin Levels During OPERA: a Real-World Study of Pegcetacoplan Treatment in US Adults With Paroxysmal Nocturnal Hemoglobinuria (PNH)
    Fishman, Jesse
    Min, Jinny
    Arnett, Lily
    Shenoy, Apeksha
    CLINICAL LYMPHOMA MYELOMA & LEUKEMIA, 2023, 23 : S363 - S363
  • [10] Pegcetacoplan for paroxysmal nocturnal hemoglobinuria
    Gerber, Gloria F.
    Brodsky, Robert A.
    BLOOD, 2022, 139 (23) : 3361 - 3365