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机构:
Childrens Hosp Westmead, Gene Therapy Res Unit, Westmead, NSW 2145, Australia
Childrens Med Res Inst, Westmead, NSW 2145, Australia
Univ Sydney, Discipline Paediat & Child Hlth, Sydney, NSW 2006, Australia Salk Inst Biol Studies, Gene Transfer Targeting & Therapeut Core, San Diego, CA USA