Bone mineral density in adult patients with pyruvate kinase deficiency on long-term mitapivat treatment

被引：1
|
作者：
Al-Samkari, Hanny [1 ]
Grace, Rachael F. [2 ]
Glenthoj, Andreas [3 ]
Andres, Oliver [4 ]
Barcellini, Wilma [5 ]
Galacteros, Frederic [6 ]
Kuo, Kevin H. M. [7 ]
Layton, D. Mark [5 ,8 ]
Morado, Marta [9 ]
Viprakasit, Vip [1 ,10 ]
Tai, Feng [1 ,11 ]
Urbstonaitis, Rolandas [1 ,11 ,12 ]
Morales, Jaime [1 ,11 ]
Mcgee, Bryan [1 ,11 ]
Beers, Eduard J. van [1 ,12 ]
机构：
[1] Harvard Med Sch, Massachusetts Gen Hosp, Div Hematol, Boston, MA 02115 USA
[2] Harvard Med Sch, Dana Farber Boston Childrens Canc & Blood Disorder, Boston, MA USA
[3] Rigshosp, Dept Hematol, Copenhagen, Denmark
[4] Univ Wurzburg, Dept Pediat, Wurzburg, Germany
[5] Fdn IRCCS Ca Granda Osped Maggiore Policlin, Milan, Italy
[6] CHU Henri Mondor, Unite Malad Genet Globule Rouge, AP HP, Creteil, France
[7] Univ Toronto, Div Hematol, Toronto, ON, Canada
[8] Hammersmith Hosp, Imperial Coll Healthcare NHS Fdn Trust, Dept Immunol & Inflammat, London, England
[9] Hosp Univ La Paz, Hematol Dept, Madrid, Spain
[10] Mahidol Univ, Siriaj Hosp, Dept Pediat, Bangkok, Thailand
[11] Agios Pharmaceut Inc, Cambridge, MA USA
[12] Univ Utrecht, Univ Med Ctr Utrecht, Ctr Benign Hematol Thrombosis & Hemostasis, Van Creveldklin, Utrecht, Netherlands
来源：
HAEMATOLOGICA | 2024年 / 109卷 / 03期
关键词：
D O I：
10.3324/haematol.2023.282884
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：963 / 967
页数：5
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