Molecular Dynamics of Genome Editing with CRISPR/Cas9 and rAAV6 Virus in Human HSPCs to Treat Sickle Cell Disease

被引：0
|
作者：
Xu, Liwen [1 ]
Lahiri, Premanjali [2 ]
Skowronski, Jason [3 ]
Bhatia, Neehar [4 ]
Lattanzi, Annalisa [5 ]
Porteus, Matthew H. [6 ]
机构：
[1] Stanford Univ, Pediat, Sch Med, Stanford, CA USA
[2] Graphite Bio, Sunnyvale, CA USA
[3] Graphite Bio, South San Fransisco, CA USA
[4] Stanford Lab Cell & Gene Med, Palo Alto, CA USA
[5] Genentech Inc, South San Francisco, CA USA
[6] Stanford Univ, Sch Med, Stanford, CA USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
515
引用
收藏
页码：262 / 263
页数：2
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