Characterization of Pre-Existing Immunity to AAV5

被引：0
|
作者：
Lau, Kelly [1 ]
机构：
[1] BioMarin Pharmaceut Inc, Novato, CA USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1074
引用
收藏
页码：515 / 515
页数：1
相关论文
共 50 条
  • [1] Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A
    Klamroth, Robert
    Hayes, Gregory
    Andreeva, Tatiana
    Gregg, Keith
    Suzuki, Takashi
    Mitha, Ismail Haroon
    Hardesty, Brandon
    Shima, Midori
    Pollock, Toni
    Slev, Patricia
    Oldenburg, Johannes
    Ozelo, Margareth C.
    Stieltjes, Natalie
    Castet, Sabine-Marie
    Mahlangu, Johnny
    Peyvandi, Flora
    Kazmi, Rashid
    Schved, Jean-Francois
    Leavitt, Andrew D.
    Callaghan, Michael
    Pan-Petesch, Brigitte
    Quon, Doris, V
    Andrews, Jayson
    Trinh, Alex
    Li, Mingjin
    Wong, Wing Yen
    HUMAN GENE THERAPY, 2022, 33 (7-8) : 432 - 441
  • [2] Impact of pre-existing immunity to AAV5 on pharmacodynamics of BMN 270, an AAV5-based gene therapy for the treatment of hemophilia A
    Long, B.
    Sandza, K.
    Holcomb, J.
    Pherarolis, J.
    Crockett, L.
    Falese, L.
    Hayes, G.
    Arens, J.
    Tsuruda, L. S.
    O'Neill, C. A.
    Pryer, N.
    Fonck, C.
    Zoog, S.
    Vettermann, C.
    HAEMOPHILIA, 2018, 24 : 59 - 60
  • [3] Pre-Existing Neutralizing Antibodies to AAV2 and AAV5 in the Serum and Synovial Fluid of 20 Horses
    Ortved, Kyla F.
    Calcedo, Roberto
    Nixon, Alan J.
    MOLECULAR THERAPY, 2012, 20 : S48 - S48
  • [4] Delivery of AAV-hAADC to rats with pre-existing immunity to AAV
    Sanftner, L
    Suzuki, B
    Doroudchi, M
    Feng, L
    McClelland, A
    Forsayeth, J
    Cunningham, J
    MOLECULAR THERAPY, 2003, 7 (05) : S90 - S90
  • [5] Strategy to detect pre-existing immunity to AAV gene therapy
    Falese, L.
    Sandza, K.
    Yates, B.
    Triffault, S.
    Gangar, S.
    Long, B.
    Tsuruda, L.
    Carter, B.
    Vettermann, C.
    Zoog, S. J.
    Fong, S.
    GENE THERAPY, 2017, 24 (12) : 768 - 778
  • [6] A Novel Strategy to Circumvent Pre-Existing Humoral Immunity to AAV
    Mingozzi, Federico
    Anguela, Xavier M.
    Pavani, Giulia
    Chen, Yifeng
    Davidson, Robert J.
    Hui, Daniel J.
    Hinderer, Christian J.
    Faella, Armida
    Howard, Crolann
    Tai, Alex
    Podsakoff, Gregory M.
    Ragni, Margaret V.
    Zhou, Shangzhen
    Basner-Tschakarjan, Etiena
    Wright, J. Fraser
    High, Katherine A.
    BLOOD, 2012, 120 (21)
  • [7] Strategy to detect pre-existing immunity to AAV gene therapy
    L Falese
    K Sandza
    B Yates
    S Triffault
    S Gangar
    B Long
    L Tsuruda
    B Carter
    C Vettermann
    S J Zoog
    S Fong
    Gene Therapy, 2017, 24 : 768 - 778
  • [8] Characterization of Human Pre-Existing Cellular Immunity against Aav 2, 4, 5, 8 and 9 Serotypes
    Xicluna, Rebecca
    Devaux, Marie
    Couzinie, Celia
    Jaulin, Nicolas
    Vandamme, Celine
    Adjali, Oumeya
    MOLECULAR THERAPY, 2018, 26 (05) : 109 - 109
  • [9] Pre-existing immunity to AAV overcome by in silico ancestral capsid design
    Zinn, E.
    Khaychuk, V.
    Sarkar, D.
    Carvalho, L.
    Pacouret, S.
    Morris, H.
    Plovie, E.
    Vandenberghe, Luk H.
    HUMAN GENE THERAPY, 2014, 25 (11) : A8 - A8
  • [10] Overcoming Pre-Existing Humoral Immunity to AAV Using Capsid Decoys
    Mingozzi, Federico
    Anguela, Xavier M.
    Pavani, Giulia
    Chen, Yifeng
    Davidson, Robert H.
    Hui, Daniel H.
    Yazicioglu, Mustafa
    Elkouby, Liron
    Hinderer, Christian J.
    Faella, Armida
    Howard, Carolann
    Tai, Alex
    Podsakoff, Gregory M.
    Ragni, Margaret C.
    Zhou, Shangzhen
    Basner-Tschakarjan, Etiena
    Wright, J. Fraser
    High, Katherine A.
    MOLECULAR THERAPY, 2013, 21 : S45 - S45
12345