Mission possible: Gene therapy for inherited metabolic diseases

被引：2
|
作者：
Baruteau, Julien [1 ,2 ,3 ,5 ]
Keshavan, Nandaki [1 ,2 ]
Venditti, Charles P. [4 ]
机构：
[1] UCL, Great Ormond St Inst Child Hlth, London, England
[2] Great Ormond St Hosp Sick Children, London, England
[3] Great Ormond St Biomed Res Ctr, Natl Inst Hlth Res, London, England
[4] NHGRI, Metab Med Branch, NIH, Bethesda, MD USA
[5] Great Ormond St Biomed Res Ctr, Natl Inst Hlth Res, London WC1N 1EH, England
来源：
JOURNAL OF INHERITED METABOLIC DISEASE | 2024年 / 47卷 / 01期
关键词：
D O I：
10.1002/jimd.12708
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：5 / 6
页数：2
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