Safety and efficacy study of taliglucerase alfa in Gaucher disease type 3: A 12-month multi-center trial

被引：0
|
作者：
Istaiti, Majdolen Joleen [1 ]
Revel-Vilk, Shoshana [1 ]
Ezgu, Fatih S. [2 ]
Gupt, Neerja [3 ]
Jana, Manisha [3 ]
Zimran, Ari [1 ]
Kabra, Madhulika [3 ]
机构：
[1] Shaare Zedek Med Ctr, Jerusalem, Israel
[2] Gazi Univ Hosp, Ankara, Turkiye
[3] All India Inst Med Sci, New Delhi, India
来源：
MOLECULAR GENETICS AND METABOLISM | 2025年 / 144卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2024.108777
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
150
引用
收藏
页数：2
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