Prime editing precisely corrects prevalent pathogenic mutations observed in glycogen storage disease type 1b (GSD1b) patients

被引：0
|
作者：
Winnay, J. [1 ]
Hart, C. [1 ]
Turna, H. [1 ]
Collias, D. [1 ]
Hernandez, S. [1 ]
Kyrychenko, S. [1 ]
Waterman, D. [1 ]
Levy, J. [1 ]
Roy, M. [1 ]
Hatit, M. [1 ]
Alexander, S. [1 ]
Ge, P. [1 ]
Geddes, B. [1 ]
Duffield, J. S. [1 ]
机构：
[1] Prime Med, Cambridge, MA USA
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR79
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页码：A38 / A38
页数：1
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