Exploiting chimeric GALC enzymes with improved bioavailability to refine gene therapy approaches for globoid cell leukodystrophy

被引：0
|
作者：
Cascino, F. [1 ]
Ricca, A. [1 ]
Picciotti, I. [1 ,2 ]
Morena, F. [3 ]
Martino, S. [3 ]
Gritti, A. [1 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy
[2] Univ Vita Salute San Raffaele, Milan, MI, Italy
[3] Univ Perugia, Dept Chem Biol & Biotechnol, Perugia, Italy
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P580
引用
收藏
页码：A248 / A248
页数：1
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