Demonstration of the Feasibility of AAV Vector-Mediated Gene Therapy for Alport Syndrome Using a Newly Established Floxed Mouse Model

被引：0
|
作者：
Das, Ranjan [1 ]
Furusho, Taisuke [1 ]
Sairavi, Anusha [1 ]
Hakui, Hideyuki [1 ]
Luo, Shuhua [1 ]
Li, Lena [1 ]
Miner, Jeffrey H. [2 ]
Nakai, Hiroyuki [1 ,3 ]
机构：
[1] Oregon Hlth & Sci Univ, Mol & Med Genet, Portland, OR USA
[2] Washington Univ, Div Nephrol, Sch Med, St Louis, MO USA
[3] Oregon Hlth & Sci Univ, Mol Microbiol & Immunol, Portland, OR USA
来源：
MOLECULAR THERAPY | 2024年 / 32卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1584
引用
收藏
页码：739 / 740
页数：2
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